IONS - Ionis Pharmaceuticals' Rare Metabolic Disorder Candidate Poised To Become New Standard Treatment Study Shows Encouraging Action | Benzinga
Ionis Pharmaceuticals Inc (NASDAQ: IONS) released topline results for the Phase 3 Balance study of olezarsen in people with familial chylomicronemia syndrome (FCS), a hereditary disease that prevents the body from breaking down fats.
The trial met its primary efficacy endpoint with a statistically significant reduction in triglyceride (TG) levels with the olezarsen 80 mg monthly dose at six months compared to placebo (p=0.0009); triglyceride lowering continued to improve ...