FOLD - Amicus Therapeutics Drug Scores FDA Approval For Rare Inherited Pompe Disease | Benzinga
The FDA has approved Amicus Therapeutics' (NASDAQ: FOLD) Pombiliti (cipaglucosidase alfa-atga)+Opfolda (miglustat) 65mg capsules for Pompe disease.
It's a disease in which the body can't make a protein that breaks down a complex sugar called glycogen for energy. Too much sugar builds up and damages muscles and organs.
This two-component therapy is indicated for adults living with late-onset ...